Successful bone marrow transplantation in a patient with Schimke immuno-osseous dysplasia.

Petty, E M; Yanik, G A; Hutchinson, R J; Alter, B P; Schmalstieg, F C; Levine, J E; Ginsburg, D; Robillard, J E et al. · J Pediatr · 2000

case_report · Level V

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Abstract

Early death in Schimke immuno-osseous dysplasia often results from renal failure and/or cell-mediated immunodeficiency. Kidney transplants have improved renal function, but effective therapy for the immunodeficiency has not yet been reported. We describe markedly improved marrow function 2 years after bone marrow transplantation in a boy with Schimke immunoosseous dysplasia.

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