Adult onset glutaric aciduria type I presenting with a leukoencephalopathy.

Bähr, O; Mader, I; Zschocke, J; Dichgans, J; Schulz, J B · Neurology · 2002

case_report · Level V

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Abstract

Glutaric aciduria type I usually presents with an acute metabolic crisis during infancy. The authors report a previously healthy 19-year-old woman who presented with recurrent headaches, oculomotor symptoms, and a severe leukoencephalopathy on MRI. The diagnosis was made by urinary organic acid analysis and confirmed by enzyme studies. Genetic analysis revealed compound heterozygosity with a deletion c.219delC in exon 3 and a novel missense mutation R132G in exon 5 of the glutaryl CoA dehydrogenase (GCDH) gene.

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