Complex phenotypes in an Indian family with homozygous SCA2 mutations.

Ragothaman, Mona; Sarangmath, Nagaraja; Chaudhary, Shashi; Khare, Vishwamohini; Mittal, Uma; Sharma, Sangeeta; Komatireddy, Sreelatha; Chakrabarti, Subhabrata et al. · Ann Neurol · 2004

case_report · Level V

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Abstract

We describe a consanguineous Indian family having spinocerebellar ataxia type 2 (SCA2) expansions with complex phenotypes (early-onset, dopa-responsive parkinsonism, ataxia and retinitis pigmentosa). The two probands having homozygous SCA2 mutations presenting with early-onset dopa-responsive parkinsonism without ataxia develop dyskinesias within a year of starting levodopa. Their siblings, heterozygous for SCA2 mutations, had retinitis pigmentosa with or without ataxia. Approximately 38% of family members with SCA2 mutations were asymptomatic.

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