Identification of a SACS gene missense mutation in ARSACS.

Ogawa, T; Takiyama, Y; Sakoe, K; Mori, K; Namekawa, M; Shimazaki, H; Nakano, I; Nishizawa, M · Neurology · 2004

case_report · Level V

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Abstract

The authors describe two patients in a Japanese family with autosomal recessive spastic ataxia of Charlevoix-Saguenay. They presented early onset spastic ataxia, sensorimotor neuropathy, nystagmus, slurred speech, and hypermyelinated retinal nerve fibers. The authors identified a homozygous missense mutation (T7492C) in the SACS gene, which resulted in the substitution of arginine for tryptophan at amino acid residue 2498 (W2498R).

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