POMT1 mutation results in defective glycosylation and loss of laminin-binding activity in alpha-DG.

Kim, D S; Hayashi, Y K; Matsumoto, H; Ogawa, M; Noguchi, S; Murakami, N; Sakuta, R; Mochizuki, M et al. · Neurology · 2004

case_report · Level V

Where this comes from

Abstract

Walker-Warburg syndrome (WWS) is a congenital muscular dystrophy associated with neuronal migration disorder and structural eye abnormalities. The mutations in the O-mannosyltransferase 1 gene (POMT1) were identified recently in 20% of patients with WWS. The authors report on a patient with WWS and a novel POMT1 mutation. Their patient expressed alpha-dystroglycan (alpha-DG) core protein, but fully glycosylated alpha-DG antibody epitopes were absent, associated with the loss of laminin-binding activity.

Medical subject headings