Coincidence of two genetic forms of Charcot-Marie-Tooth disease in a single family.

Verny, C; Ravisé, N; Leutenegger, A-L; Pouplard, F; Dubourg, O; Tardieu, S; Dubas, F; Brice, A et al. · Neurology · 2004

case_report · Level V

Where this comes from

Abstract

The authors report a family in which two affected first cousins had a severe demyelinating Charcot-Marie-Tooth disease (CMT) phenotype. One had related parents, and there were no other affected relatives, suggesting an autosomal recessive mode of inheritance. Molecular studies showed that a de novo duplication in 17p11.2 and a second mutation in MTMR2 were present.

Medical subject headings