POLG mutations in Alpers syndrome.

Nguyen, K V; Østergaard, E; Ravn, S Holst; Balslev, T; Danielsen, E Rubaek; Vardag, A; McKiernan, P J; Gray, G et al. · Neurology · 2005

case_series · Level IV

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Abstract

Described are six patients with Alpers syndrome from four unrelated families. Affected individuals harbored the following combinations of POLG mutations: 1) A467T/W1020X, 2) W748S-E1143G/G848S, 3) A467T/A467T, and 4) A467T/G848S. Homozygosity for the A467T allele in one patient was associated with a later age at onset. Mitochondrial respiratory chain studies in skeletal muscle were normal in each case. Nine combinations of mutant POLG alleles that cause Alpers syndrome are summarized.

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