Commissioning for rare diseases: view from the frontline.

Burls, Amanda; Austin, Daphne; Moore, David · BMJ · 2005

review · Level V

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Abstract

Deciding whether to fund treatments that do good one by one tends to lead to a positive decision. However, this can cause wider harmful effects, as West Midlands' experience in the funding of enzyme replacement therapy for lysosomal storage diseases shows

Medical subject headings