Coexistence of CMT-2D and distal SMA-V phenotypes in an Italian family with a GARS gene mutation.

Del Bo, R; Locatelli, F; Corti, S; Scarlato, M; Ghezzi, S; Prelle, A; Fagiolari, G; Moggio, M et al. · Neurology · 2006

case_report · Level V

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Abstract

An Italian multigenerational family with four members affected by an axonal Charcot-Marie-Tooth type 2D (CMT-2D) or distal spinal muscular atrophy (dSMA) phenotype with upper limb predominance, variable age at onset, degree of disability, and autosomal dominant inheritance is reported. A novel heterozygous missense GARS gene mutation (D500N) was identified.

Medical subject headings