Gaucher disease: progressive mesenteric and mediastinal lymphadenopathy despite enzyme therapy.

Burrow, T Andrew; Cohen, Mitchell B; Bokulic, Ronald; Deutsch, Gail; Choudhary, Arabinda; Falcone, Richard A; Grabowski, Gregory A · J Pediatr · 2007

case_report · Level V

Where this comes from

Abstract

A 5-year-old male with Gaucher's disease type 3 developed progressive mesenteric and mediastinal lymphadenopathy over 12 months, despite enzyme replacement therapy, contributing to the development of a protein-losing enteropathy. These complications are unique, indicating poorly accessible, differentially responsive compartments in patients with Gaucher's disease who are receiving enzyme therapy.

Medical subject headings