Novel de novo large deletion in cystic fibrosis transmembrane conductance regulator gene results in a severe cystic fibrosis phenotype.

Norek, Aleksandra; Stremska, Marta; Sobczyńska-Tomaszewska, Agnieszka; Wertheim-Tysarowska, Katarzyna; Dmeńska, Hanna; Jurek, Marta · J Pediatr · 2011

case_report · Level V

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Abstract

We identified c.1521_1523delCTT and c.1679+94_2619+986del8118 in trans in a 6-year-old boy with a severe cystic fibrosis phenotype. The first deletion was inherited maternally, but the latter had arisen de novo.

Medical subject headings