Novel overgrowth syndrome phenotype due to recurrent de novo PDGFRB mutation.

Takenouchi, Toshiki; Yamaguchi, Yu; Tanikawa, Akiko; Kosaki, Rika; Okano, Hideyuki; Kosaki, Kenjiro · J Pediatr · 2015

case_report · Level V

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Abstract

Using exome analysis, we identified a novel overgrowth syndrome arising from a mutation in PDGFRB, which plays a critical role in growth and differentiation. This entity is characterized by somatic overgrowth, distinctive facial features, hyperelastic and fragile skin, white matter lesions, and neurologic deterioration.

Medical subject headings