Lethal Disorder of Mitochondrial Fission Caused by Mutations in DNM1L.

Yoon, Grace; Malam, Zeenat; Paton, Tara; Marshall, Christian R; Hyatt, Ella; Ivakine, Zhenya; Scherer, Stephen W; Lee, Kyong-Soon et al. · J Pediatr · 2016

case_report · Level V

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Abstract

We describe two infants with hypotonia, absent respiratory effort, and giant mitochondria in neurons due to compound heterozygosity for 2 nonsense mutations of DNM1L. DNM1L has a critical role in regulating mitochondrial morphology and function. This observation confirms the central role of mitochondrial fission to normal human development.

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