Imprecision Medicine: A One-Size-Fits-Many Approach for Muscle Dystrophy.
editorial · Level V
Where this comes from
- Record sourced from PubMed, PMID 27058929.
- Also identified by DOI 10.1016/j.stem.2016.03.004.
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Abstract
There is still no curative treatment for Duchenne muscular dystrophy (DMD). In this issue of Cell Stem Cell, Young et al. (2016) demonstrate a genome editing approach applicable to 60% of DMD patients with CRISPR/Cas9 using one pair of guide RNAs.
Medical subject headings
- CRISPR-Cas Systems
- Dystrophin