Rounding up sickle cells with gene therapy.
case_report · Level V
Where this comes from
- Record sourced from PubMed, PMID 28298423.
- Also identified by DOI 10.1126/scitranslmed.aam9864.
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Abstract
A report of a patient treated with ex vivo lentiviral gene transfer to hematopoietic stem cells shows the promise of gene therapy for sickle cell anemia.
Medical subject headings
- Anemia, Sickle Cell
- Genetic Vectors