Pulmonary Endpoints in Duchenne Muscular Dystrophy. A Workshop Summary.
review · Level V
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- Record sourced from PubMed, PMID 28636407.
- Also identified by DOI 10.1164/rccm.201703-0507WS.
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Abstract
Development of novel therapeutics for treatment of Duchenne muscular dystrophy (DMD) has led to clinical trials that include pulmonary endpoints that allow assessment of respiratory muscle status, especially in nonambulatory subjects. Parent Project Muscular Dystrophy (PPMD) convened a workshop in Bethesda, Maryland, on April 14 and 15, 2016, to summarize published respiratory data in DMD and give guidance to clinical researchers assessing the effect of interventions on pulmonary outcomes in DMD.
Medical subject headings
- Lung
- Muscular Dystrophy, Duchenne
- Respiratory Muscles