Barth Syndrome: Different Approaches to Diagnosis.

Imai-Okazaki, Atsuko; Kishita, Yoshihito; Kohda, Masakazu; Yatsuka, Yukiko; Hirata, Tomoko; Mizuno, Yosuke; Harashima, Hiroko; Hirono, Keiichi et al. · J Pediatr · 2018

case_report · Level V

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Abstract

The diagnosis of Barth syndrome is challenging owing to the wide phenotypic spectrum with allelic heterogeneity. Here we report 3 cases of Barth syndrome with phenotypic and allelic heterogeneity that were diagnosed by different approaches, including whole exome sequencing and final confirmation by reverse-transcription polymease chain reaction.

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