IKBKG (NEMO) 5' Untranslated Splice Mutations Lead to Severe, Chronic Disseminated Mycobacterial Infections.

Hsu, Amy P; Zerbe, Christa S; Foruraghi, Ladan; Iovine, Nicole M; Leiding, Jennifer W; Mushatt, David M; Wild, Laurianne; Kuhns, Douglas B et al. · Clin Infect Dis · 2018

case_series · Level IV

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Abstract

Four patients with adult-onset, disseminated mycobacterial infection had 5' UTR mutations in IKBKG without clear physical stigmata of NEMO deficiency. These mutations caused decreased levels of NEMO protein and Toll-like receptor driven cytokine production. Three patients died from disseminated disease. These mutations may be missed by whole exome sequencing.

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