Jakinibs for the treatment of immune dysregulation in patients with gain-of-function signal transducer and activator of transcription 1 (STAT1) or STAT3 mutations.

Forbes, Lisa R; Vogel, Tiphanie P; Cooper, Megan A; Castro-Wagner, Johana; Schussler, Edith; Weinacht, Katja G; Plant, Ashley S; Su, Helen C et al. · J Allergy Clin Immunol · 2018

Level V

Where this comes from

Abstract

Treatment of the autoimmune and immune-dysregulatory features of patients with STAT1 GOF or STAT3 GOF disease remains challenging. Jakinibs have been used to treat the severe immune-dysregulation in patients with either <i>STAT1</i> GOF or <i>STAT3</i> GOF mutations.

Medical subject headings