Future AAVenues for In Utero Gene Therapy.
editorial · Level V
Where this comes from
- Record sourced from PubMed, PMID 30193130.
- Also identified by DOI 10.1016/j.stem.2018.08.010.
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Abstract
Fetal gene therapy using safe and effective viral vectors no longer remains a distant prospect. Recently in Nature Medicine, Massaro et al. (2018) demonstrated that prenatal intracranial injection of a viral vector results in improved neurologic function, raising the intriguing possibility that in utero gene therapy may be approaching clinical applications.
Medical subject headings
- Neurodegenerative Diseases