Measure Twice, Cut Once: Therapeutic Editing of HSPCs Requires Precise Planning.

Rau, Rachel E; Goodell, Margaret A · Cell Stem Cell · 2019

editorial · Level V

Where this comes from

Abstract

Hematologic diseases may be among the first clinical targets for therapeutic gene editing. In this issue of Cell Stem Cell, Schiroli et al. (2019) report a thorough, unbiased investigation of the impact of gene editing on hematopoietic stem and progenitor function and offer a clear path forward for editing in multiple tissues and conditions.

Medical subject headings