Dosage Counts: Correcting Trisomy-21-Related Phenotypes in Human Organoids and Xenografts.

Manley, William F; Anderson, Stewart A · Cell Stem Cell · 2019

basic_science · Level V

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Abstract

Studies in mice suggest that Olig2 gene dosage alters cerebral cortical interneuron development and contributes to trisomy-21/Down-syndrome-related intellectual disability. Xu et al. (2019) extend these studies through the remarkable use of cerebral organoid and human iPSC/mouse brain chimera experimental systems that provide an opportunity for the development of novel therapeutics.

Medical subject headings