Gene Editing Expands the Donor Pool for CCR5-Negative Stem Cell Transplants.

Cannon, Paula M · Cell Stem Cell · 2019

editorial · Level V

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Abstract

Cell therapy efforts for treating HIV+ patients are challenged by limited availability of donors with naturally occurring CCR5 mutations conferring resistance. Xu et al. (2019) report a CRISPR-based method for disrupting CCR5 in hematopoietic stem cells prior to transplant, providing a proof of concept for expanding the pool of potential donors.

Medical subject headings