Familial Haploidentical Stem Cell Transplant in Children and Adolescents With High-Risk Sickle Cell Disease: A Phase 2 Clinical Trial.
prospective_cohort · Level II
Where this comes from
- Record sourced from PubMed, PMID 31816036.
- Also identified by DOI 10.1001/jamapediatrics.2019.4715 and PMC identifier 6902105.
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Abstract
This phase 2 clinical trial in patients with high-risk sickle cell disease assesses the feasibility, safety, and 1-year event-free survival after myeloimmunoablative conditioning and familial haploidentical stem cell transplant.
Medical subject headings
- Anemia, Sickle Cell
- Stem Cell Transplantation