Heterozygous IKKβ activation loop mutation results in a complex immunodeficiency syndrome.

Abbott, Jordan; Ehler, Angelica C; Jayaraman, Divya; Reynolds, Paul R; Otsu, Kanao; Manka, Laurie; Gelfand, Erwin W · J Allergy Clin Immunol · 2021

basic_science · Level V

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Abstract

We identified in an adult with ectodermal dysplasia and immunodeficiency a germline, gain-of-function mutation, K171R, in IKBKB. The K171R mouse immunologic phenotype parallels human, suggesting IKBKB K171R underlies a novel immunodeficiency syndrome.

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