Gene therapy for global brain diseases: one small step for mice, one giant leap for humans.
editorial · Level V
Where this comes from
- Record sourced from PubMed, PMID 32671401.
- Also identified by DOI 10.1093/brain/awaa189 and PMC identifier 7364739.
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Abstract
This scientific commentary refers to ‘Global CNS correction in a large brain model of human alpha-mannosidosis by intravascular gene therapy’, by Yoon <i>et al.</i> (doi:10.1093/brain/awaa161).
Medical subject headings
- Brain Diseases
- alpha-Mannosidosis