Targeting PIs to improve PTs:a new approach to treating genetic diseases of the proximal tubule.

Weisz, Ora A · Kidney Int · 2020

basic_science · Level V

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Abstract

Defective recycling of megalin consequent to impaired phosphatidylinositol metabolism has been implicated as a mechanism causing tubular proteinuria in patients with Lowe syndrome. In this issue, Berquez et al. describe an innovative approach using a clinically approved drug to "rebalance" phosphatidylinositols and restore megalin traffic in mouse and cell models of the disease.

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