Assessment of rAAVrh.74.MHCK7.micro-dystrophin Gene Therapy Using Magnetic Resonance Imaging in Children With Duchenne Muscular Dystrophy.
case_control · Level III
Where this comes from
- Record sourced from PubMed, PMID 33394000.
- Also identified by DOI 10.1001/jamanetworkopen.2020.31851 and PMC identifier 7783546.
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Abstract
This case-control study uses magnetic resonance imaging and spectroscopy to evaluate the association between treatment with recombinant adeno-associated virus serotype rh74 (rAAVrh74) and muscle quality in children with Duchenne muscular dystrophy.
Medical subject headings
- Dystrophin
- Genetic Therapy
- Magnetic Resonance Imaging
- Muscular Dystrophy, Duchenne