Endophilin A2 deficiency protects rodents from autoimmune arthritis by modulating T cell activation.

Norin, Ulrika; Rintisch, Carola; Meng, Liesu; Forster, Florian; Ekman, Diana; Tuncel, Jonatan; Klocke, Katrin; Bäcklund, Johan et al. · Nat Commun · 2021

basic_science · Level V

Where this comes from

Abstract

The introduction of the CTLA-4 recombinant fusion protein has demonstrated therapeutic effects by selectively modulating T-cell activation in rheumatoid arthritis. Here we show, using a forward genetic approach, that a mutation in the SH3gl1 gene encoding the endocytic protein Endophilin A2 is associated with the development of arthritis in rodents. Defective expression of SH3gl1 affects T cell effector functions and alters the activation threshold of autoreactive T cells, thereby leading to complete protection from chronic autoimmune inflammatory disease in both mice and rats. We further show that SH3GL1 regulates human T cell signaling and T cell receptor internalization, and its expression is upregulated in rheumatoid arthritis patients. Collectively our data identify SH3GL1 as a key regulator of T cell activation, and as a potential target for treatment of autoimmune diseases.

Medical subject headings