In vivo spatiotemporal control of voltage-gated ion channels by using photoactivatable peptidic toxins.

Montnach, Jérôme; Blömer, Laila Ananda; Lopez, Ludivine; Filipis, Luiza; Meudal, Hervé; Lafoux, Aude; Nicolas, Sébastien; Chu, Duong et al. · Nat Commun · 2022

basic_science · Level V

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Abstract

Photoactivatable drugs targeting ligand-gated ion channels open up new opportunities for light-guided therapeutic interventions. Photoactivable toxins targeting ion channels have the potential to control excitable cell activities with low invasiveness and high spatiotemporal precision. As proof-of-concept, we develop HwTxIV-Nvoc, a UV light-cleavable and photoactivatable peptide that targets voltage-gated sodium (Na<sub>V</sub>) channels and validate its activity in vitro in HEK293 cells, ex vivo in brain slices and in vivo on mice neuromuscular junctions. We find that HwTxIV-Nvoc enables precise spatiotemporal control of neuronal Na<sub>V</sub> channel function under all conditions tested. By creating multiple photoactivatable toxins, we demonstrate the broad applicability of this toxin-photoactivation technology.

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