Successful Elosulfase Alfa Desensitization Protocol in a Patient With Morquio A Syndrome.

Díaz Vidal, Verónica C; Gillispie, Amanda; Aranda, Carolina; Anvari, Sara · Pediatrics · 2022

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Abstract

Patients with lysosomal storage diseases may require modifications to standard drug desensitization protocols; personalized medicine as well as development of new treatment options are needed.

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