Methamphetamine enhances caveolar transport of therapeutic agents across the rodent blood-brain barrier.

Chang, Jui-Hsien; Greene, Chris; Frudd, Karen; Araujo Dos Santos, Leonardo; Futter, Clare; Nichols, Benjamin J; Campbell, Matthew; Turowski, Patric · Cell Rep Med · 2022

basic_science · Level V

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Abstract

The blood-brain barrier (BBB) restricts clinically relevant accumulation of many therapeutics in the CNS. Low-dose methamphetamine (METH) induces fluid-phase transcytosis across BBB endothelial cells <i>in vitro</i> and could be used to enhance CNS drug delivery. Here, we show that low-dose METH induces significant BBB leakage in rodents <i>ex vivo</i> and <i>in vivo</i>. Notably, METH leaves tight junctions intact and induces transient leakage via caveolar transport, which is suppressed at 4°C and in caveolin-1 (CAV1) knockout mice. METH enhances brain penetration of both small therapeutic molecules, such as doxorubicin (DOX), and large proteins. Lastly, METH improves the therapeutic efficacy of DOX in a mouse model of glioblastoma, as measured by a 25% increase in median survival time and a significant reduction in satellite lesions. Collectively, our data indicate that caveolar transport at the adult BBB is agonist inducible and that METH can enhance drug delivery to the CNS.

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