Use of External Control Cohorts in Pediatric Brain Tumor Clinical Trials.

Margol, Ashley S; Molinaro, Annette M; Onar-Thomas, Arzu; Resnick, Adam; Hanson, Derek; Kieran, Mark; Mishra-Kalyani, Pallavi; Rivera, Donna et al. · J Clin Oncol · 2024

review · Level V

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Abstract

Why, when, and how to consider external control cohorts in pediatric brain tumor clinical trials.

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