Different factors underlie mild and severe forms of spinal muscular atrophy.

Ottesen, Eric W; Singh, Ravindra N · Brain · 2025

editorial · Level V

Where this comes from

Abstract

This scientific commentary refers to ‘The systemic complexity of a monogenic disease: the molecular network of spinal muscular atrophy’ by Tapken <i>et al.</i> (https://doi.org/10.1093/brain/awae272).