Biallelic variants in SREK1 downregulating SNORD115 and SNORD116 cause a Prader-Willi-like syndrome.

Saeed, Sadia; Siegert, Anna-Maria; Tung, Y C Loraine; Khanam, Roohia; Janjua, Qasim M; Manzoor, Jaida; Derhourhi, Mehdi; Toussaint, Bénédicte et al. · J Clin Invest · 2025

case_series · Level IV

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Abstract

Biallelic variations in SREK1 reduce SNORD115/116 expression, linking severe obesity and Prader-Willi-like traits, offering genetic and molecular insights into a new form of syndromic obesity.

Medical subject headings