How to create personalized gene editing platforms: Next steps toward interventional genetics.

Ahrens-Nicklas, Rebecca C; Musunuru, Kiran · Am J Hum Genet · 2025

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Abstract

How do we go from a single individual receiving a personalized gene-editing therapy to a future of "interventional genetics" in which such therapies are the standard of care? First and foremost: regulatory innovation.

Medical subject headings