A degron-mimicking molecular glue drives CRBN homo-dimerization and degradation.

Langousis, Gerasimos; Gainza, Pablo; Hunkeler, Moritz; Kapsitidou, Despoina; Donckele, Etienne J; Annunziato, Stefano; Wiedmer, Lars; Jones, Katherine F M et al. · Nat Commun · 2025

basic_science · Level V

Where this comes from

Abstract

Cereblon (CRBN) is an E3 ubiquitin ligase widely harnessed for targeted protein degradation (TPD). We report the discovery of a molecular glue degrader (MGD), MRT-31619, that drives homo-dimerization of CRBN and promotes its fast, potent, and selective degradation by the ubiquitin proteasome system. Interestingly, the cryo-electron microscopy (cryo-EM) structure of the CRBN homodimer reveals a unique mechanism whereby two molecular glues assemble into a helix-like structure and drive ternary complex formation by mimicking a neosubstrate G-loop degron. This CRBN chemical knockout offers a valuable tool to elucidate the molecular mechanism of MGDs, to investigate its endogenous substrates and understand their physiological roles.

Medical subject headings