Targeting modulated vascular smooth muscle cells in atherosclerosis via FAP-directed immunotherapy.

Amrute, Junedh M; Jung, In-Hyuk; Yamawaki, Tracy; Lin, Wen-Ling; Bredemeyer, Andrea; Diekmann, Johanna; Hayat, Sikander; Zhang, Xianglong et al. · Science · 2026

basic_science · Level V

Where this comes from

Abstract

Vascular smooth muscle cell (VSMC) diversification drives atherosclerotic coronary artery disease (CAD). Mechanisms governing these cell state transitions remain unclear. We applied multiomic single-cell profiling, epitope mapping, and spatial transcriptomics across 27 human coronary arteries, identifying fibroblast activation protein (FAP) as a marker of modulated VSMCs. Lineage tracing in mice indicated that FAP<sup>+</sup> cells originate from <i>Myh11</i><sup>+</sup> VSMCs, and FAP PET imaging in CAD patients showed plaque uptake. FAP<sup>+</sup> cells states resided in the macrophage-rich neo-intima. Therapeutically, we developed an anti-FAP bispecific T-cell engager, which reduced plaque burden and remodeled the stromal-immune microenvironment through T-cell clonal expansion. Our study delivers a single-cell and spatial atlas of human CAD, establishes FAP as a marker of modulated VSMCs, and highlights immunotherapy for lipid-independent targets.