Luspatercept ameliorates disease phenotype and complications in the Townes mouse model of sickle cell disease.

Sezaki, Maiko; Li, Tian; Pan, Mingzhe; Wang, Zhihong; Bai, Jie; Horowitz, Justin G; Xu, Julia Z; Huang, Gang · J Clin Invest · 2026

basic_science · Level V

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Abstract

Preclinical data demonstrating that luspatercept mitigates vaso-occlusive and anemia-related complications in the Townes sickle cell model provide a strong rationale for its evaluation in SCD patients.

Medical subject headings