Recurrent metabolic decompensation in profound carnitine palmitoyltransferase II deficiency.

Elpeleg, O N; Joseph, A; Branski, D; Christensen, E; Holme, E; Demaugre, F; Saudubray, J M; Gutman, A · J Pediatr · 1993

case_report · Level V

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Abstract

A 3-year-old boy had recurrent episodes of lethargy, encephalopathy, and hepatomegaly accompanied by hypoglycemia, elevated liver aminotransferase and creatine kinase values, and nonketotic dicarboxylic aciduria; the serum carnitine level was moderately reduced. Carnitine palmitoyltransferase II activity was decreased in lymphocytes and fibroblasts. Therapy with L-carnitine and a diet low in long-chain triglycerides did not prevent recurrent episodes.

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