Early and severe sensory loss in three adult siblings with hexosaminidase A and B deficiency (Sandhoff disease).

Schnorf, H; Gitzelmann, R; Bosshard, N U; Spycher, M; Waespe, W · J Neurol Neurosurg Psychiatry · 1995

case_report · Level V

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Abstract

Three siblings in their sixth and seventh decade with hexosaminidase A and B deficiency (adult form of GM2-gangliosidosis, variant O) developed early and severe sensory loss in addition to chronic motor neuron disease and cerebellar ataxia. Prominent mechanoallodynia was a manifesting symptom in two siblings. It is suggested that sensory deficits are due to a central-peripheral dying back axonopathy. The early and dominant sensory disturbances extend the clinical range of GM2-gangliosidosis.

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