Hypoparathyroidism in mitochondrial trifunctional protein deficiency.

Dionisi-Vici, C; Garavaglia, B; Burlina, A B; Bertini, E; Saponara, I; Sabetta, G; Taroni, F · J Pediatr · 1996

case_report · Level V

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Abstract

Mitochondrial trifunctional protein deficiency, a recently identified disorder of fatty-acid oxidation, may show characteristic features such as peripheral neuropathy, pigmentary retinopathy, and acute fatty liver degeneration in pregnant women with an affected fetus. We describe a patient with trifunctional protein deficiency whose clinical picture consisted of severe calcium and phosphate abnormalities caused by hypoparathyroidism.

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