Immunoablation does not delay the neurologic progression of X-linked adrenoleukodystrophy.

Nowaczyk, M J; Saunders, E F; Tein, I; Blaser, S I; Clarke, J T · J Pediatr · 1997

case_report · Level V

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Abstract

We report the results of a near total myeloablation in preparation for bone marrow transplantation in a boy with minimal symptoms of X-linked adrenoleukodystrophy. Severe cerebral X-linked adrenoleukodystrophy developed in the patient after failure of bone marrow transplantation. This experience suggests that immunotherapy alone is not responsible for the improvement observed in some patients with X-ALD after BMT.

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