Bone marrow transplantation for the treatment of alpha-mannosidosis.

Wall, D A; Grange, D K; Goulding, P; Daines, M; Luisiri, A; Kotagal, S · J Pediatr · 1998

case_report · Level V

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Abstract

We report successful bone marrow transplantation in a child with a severe form of alpha-mannosidosis, type I. There was complete resolution of the recurrent sinopulmonary disease and organomegaly, improvement in the bony disease, and stabilization of neurocognitive function.

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